Acadia Pharmaceuticals Inc. (Nasdaq: ACAD) today announced that the journal Med published results from the open-label study, DAFFODIL™, evaluating the safety, tolerability and exploratory efficacy of ...
Rett syndrome is a rare genetic disease affecting 1 in 10,000 newborn girls, characterized by sudden regression around 1 year ...
At just 26 months old, Grace Visser was diagnosed with Rett Syndrome, a rare genetic disorder that affects brain development.
Minoryx Therapeutics, a late-stage biotech company focused on the development of therapies for orphan central nervous system (CNS) disorders, today announces that the first patient in the TREE study ...
Heading the BNA2025? We've gone through the scientific program to find the sessions we think the BioTechniques audience will ...
Scientists have uncovered how mutations in the MeCP2 gene lead to Rett syndrome, a devastating neurological disorder. By ...
New research brings scientists one step closer to understanding Rett Syndrome, a rare genetic disease that affects 1 in ...
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Neurotech International has received positive feedback from the European Medicines Agency (EMA) on the company’s Orphan ...
Biomed Industries, Inc. to Announce Phase 2/3 Results of NA-921 for the treatment of Rett Syndrome at the IRSF Rett Syndrome Scientific conference 2025 The Phase 2/3 results of NA-921 shows strong ...
Researchers at the Josep Carreras Leukaemia Research Institute revealed a new aspect of Rett Syndrome’s pathogenesis that can ...
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