The FDA granted orphan drug designation to Sineugene Therapeutics' SNUG01, a first-in-class experimental gene therapy for ...

DCC gives nod to amend Rules related to licensing of stem cell derived & gene therapy products: Gireesh Babu, New Delhi Monday, July 7, 2025, 08:00 Hrs [IST] The Drugs Consultativ ...

Rett syndrome is a devastating rare genetic childhood disorder primarily affecting girls. Merely 1 out of 10,000 girls are ...

Using an AI-driven drug discovery process, the drug known as vorinostat was identified as a promising treatment for Rett ...

The GOP tax bill repeals the Inflation Reduction Act’s price controls for drugs for rare diseases.

Gabriella Ngang, of Farmington Hills, is one of three in Michigan to take part in a clinical trial of a new sickle cell ...

Researchers at the Gray Faculty of Medical and Health Sciences at Tel Aviv University have developed a model that accurately ...

Tissue samples sent to the International Space Station reveal what can happen to astronauts on long-term missions.

Ajay Sood emphasized the need for affordable cell and gene therapies in India, suggesting a national mission to drive down ...

A recent study involving researchers from the University of Basel reveals that slowing down the intracellular transport of ...

Rett syndrome is a devastating rare genetic childhood disorder primarily affecting girls. Merely 1 out of 10,000 girls are ...