Spirovant Sciences achieves milestone for experimental cystic fibrosis treatment
The firm's chief scientific officer called the achievement "a major milestone for Spirovant and for the cystic fibrosis ...
STAT1d
The health care system is ill-equipped to recognize and treat cystic fibrosis in non-white patients
Rena Barrow has two sons with cystic fibrosis, born 20 years apart — but they faced the same terrible delay in diagnosis.
ReCode to secure funds for cystic fibrosis gene correction treatments
ReCode Therapeutics is set to secure up to $15m in additional funding from the Cystic Fibrosis Foundation to enhance its gene ...
Leader-Post on MSN1d
Cystic fibrosis drug now available to more people in Saskatchewan
Cystic Fibrosis Canada (CFC) is celebrating the recommendation to expand coverage to patients with at least one of 152 rare ...
westcentralonline1d
Saskatchewan expands access to life-changing cystic fibrosis drug
More cystic fibrosis (CF) patients in Saskatchewan now have access to Trikafta, a groundbreaking medication that improves ...
Spirovant Sciences doses first subject in cystic fibrosis gene therapy trial
"Spirovant Sciences doses first subject in cystic fibrosis gene therapy trial" was originally created and published by ...
Business Wire4d
ReCode Therapeutics Announces Additional Funding From the Cystic Fibrosis Foundation to Accelerate Development of Novel Gene Correction Therapeutics to Treat Cystic Fibrosis
About Cystic Fibrosis Cystic fibrosis (CF) is a progressive genetic disease that causes persistent lung infections and respiratory failure. CF is caused by mutations in the cystic fibrosis ...
Cystic Fibrosis Foundation4d
CF Foundation Invests Up to $15 million in ReCode Therapeutics to Develop a Gene Editing Therapy
The Cystic Fibrosis Foundation is funding the development of a gene editing therapy that is designed to use ReCode’s tissue-specific delivery vehicle to transport gene editing cargo to the lung cells ...
BBC22d
Brother died waiting for lung transplant, says campaigner
Cahir O’Hagan from Clonoe in County Tyrone was 25 years old when he died waiting for a double lung transplant. He had cystic fibrosis, external (CF), an inherited condition that causes sticky ...
Palm Beach Post19d
Mother watches girl find life, love, baking despite cystic fibrosis — and then time ran out
A baby born today with the recessive-gene mutation that causes cystic fibrosis has the chance to live into his or her 50s and beyond. Thanks to advances in DNA testing, doctors are identifying ...
Advocacy results in access to life-saving drugs
Helping children aged two to five with the most common CF mutation gain access to the life-changing treatment, Trikafta, as a ...