Spinal muscular atrophy (SMA) is a progressive neuromuscular disorder caused by mutations in SMN1, with disease severity influenced by the number of SMN2 copies. Although SMA is one of the most common ...
Back to Healio In 2024, Healio covered several stories about trials investigating geographic atrophy biomarkers and treatment options. While one trial found that intravitreal pegcetacoplan showed ...