At just 26 months old, Grace Visser was diagnosed with Rett Syndrome, a rare genetic disorder that affects brain development.

Minoryx Therapeutics, a late-stage biotech company focused on the development of therapies for orphan central nervous system (CNS) disorders, today announces that the first patient in the TREE study ...

Biomed Industries, Inc. to Announce Phase 2/3 Results of NA-921 for the treatment of Rett Syndrome at the IRSF Rett Syndrome Scientific conference 2025 The Phase 2/3 results of NA-921 shows strong ...

Neurotech International has received positive feedback from the European Medicines Agency (EMA) on the company’s Orphan ...

Q4 2024 Earnings Call Transcript February 26, 2025 Taysha Gene Therapies, Inc. beats earnings expectations. Reported EPS is $ ...

Healthcare analysts believe that shares in rare neurological share play Neuren Pharmaceuticals are well undervalued after a ...

Acadia is seeing solid growth from its two products on the market. Check out the analysis of ACAD stock following Q4 numbers ...

A Springfield, Ohio, skating rink has come under fire after its owners denied entry to a diabetic 6-year-old boy and his service dog in violation of ADA laws.

Y Intercept Hong Kong Ltd purchased a new position in Anavex Life Sciences Corp. (NASDAQ:AVXL – Free Report) during the 4th ...

When Ms. Liu, a cancer patient, picked up a box of medication at the hospital pharmacy, she felt an overwhelming sense ...