High levels of ammonia kill liver cells by damaging the mitochondria that power the cells. But this can be prevented using an ...
Scientists have uncovered how ammonia wreaks havoc on liver cells by damaging mitochondria, leading to a dangerous cycle of toxicity. This discovery provides new hope as an existing drug, YAQ-005, ...
High levels of ammonia kill liver cells by damaging the mitochondria that power the cells. But this can be prevented using an existing drug due to ...
Many Vietnamese children are now born fully healthy thanks to a gene decoding technology used by Prof Dr Tran Van Khanh in ...
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GlobalData on MSNZevra sells priority review voucher for $150m to support drug launchesZevra has sold its US Food and Drug Administration (FDA) priority review voucher (PRV) for $150m to an undisclosed party. The ...
For Zevra Therapeutics, last year’s approval of the rare lysosomal storage disorder drug Miplyffa appears to be the gift that ...
In May 2023, the World Health Organization (WHO) declared the COVID-19 global health emergency over. Yet millions of people still experience fatigue, breathlessness and pain, years after having a ...
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GlobalData on MSNInborn errors of metabolism elicit unique challenges for therapy developmentAs Rare Disease Day is commemorated on 28 February, experts discuss the barriers to gene therapy access for some rare ...
We recently published a list of 12 Penny Stocks with Insider Buying in 2025. In this article, we are going to take a look at ...
The benefit of 4-PBA is it is already approved by drug regulators like the US Food and Drug Administration (FDA) to treat urea cycle disorders. This means it has already been deemed safe to use as ...
In May 2023, the World Health Organization (WHO) declared the COVID-19 global health emergency over. Yet millions of people still experience fatigue, breathlessness and pain, years after having a ...
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