Gabriella Ngang, of Farmington Hills, is one of three in Michigan to take part in a clinical trial of a new sickle cell ...

Boosting Klotho protein levels in mice improves physical and cognitive aging, offering potential for future longevity ...

A new study led by UC San Diego’s Scripps Institution of Oceanography may pave the way for lab-based production of rare coral ...

A researcher says an experimental gene therapy for a rare inherited disorder is saving almost as much money for the treatment ...

The GOP tax bill repeals the Inflation Reduction Act’s price controls for drugs for rare diseases.

New technologies and a proactive mindset are transforming how glaucoma is diagnosed and treated—and redefining what ...

Using an AI-driven drug discovery process, the drug known as vorinostat was identified as a promising treatment for Rett ...

Rett syndrome is a devastating rare genetic childhood disorder primarily affecting girls. Merely 1 out of 10,000 girls are ...

The manure of farmyard animals such as pigs is a major source of antibiotic-resistance genes, which can pose a risk to human ...

Rett syndrome is a devastating rare genetic childhood disorder primarily affecting girls. Merely 1 out of 10,000 girls are ...

The research reveals how targeting the KMT2D gene could help correct oral disorders and prevent craniofacial birth defects.

A strategy that analyzes the structural properties of RNA could help identify regions that are promising targets for antiviral drugs.