Gene-editing therapies—techniques that modify DNA to treat or prevent disease—have the potential to transform the field of ...

The increasing complexity of emerging therapies and the need for faster development have led to the adoption of advanced ...

After 44 days, Kendric Cromer, 12, left the hospital. While his family feels fortunate that he was the first to receive a ...

As Shift Bioscience raises $16 million in seed funding, delve into the field of cellular reprogramming to tackle age-related ...

Confounding data from a Pfizer clinical trial have rattled the field of gene therapy for Duchenne muscular dystrophy ...

Researchers identified key gene expression differences in addiction-relevant brain regions that provide new insights into ...

All cancer mutations that cause drug resistance fall into one of four categories. New research has detailed each type, helping to uncover targets for drug development and identify potential effective ...

Gene therapy could help obese kids avoid health problems associated with excess weight, including arthritis, a new study ...

The first patient has been dosed in an open-label Phase 1/2 clinical trial of AMT-162, uniQure's one-time gene therapy for ...

The number of U.S. children who suffer seizures after swallowing prescription medications or illicit drugs has doubled in ...

In 2020, life expectancy for people with cystic fibrosis was just 36. A new drug available on the NHS may be about to change ...

Discovered 30 years ago, microRNAs are increasingly recognized as important regulators of cell physiology and human disease.