Beta thalassemia: This type of thalassemia is caused ... Fatigue • Weakness • Pale skin • Shortness of breath Causes of thalassemiaThalassemia is an inherited blood disorder.

Needles and tubes no longer faze Puttinant Rungsunlohakul, nor do bags of deep red blood. For most of his life, the ...

researchers in China surprised everyone by announcing that they had used CRISPR in nonviable human embryos to try to fix the genetic defect that causes beta-thalassemia, a potentially fatal blood ...

Detroit — The Detroit Medical Center has begun treating patients with the first gene therapy for beta-thalassemia, a rare blood disorder that causes anemia and often requires regular blood ...

In that spirit, let's discuss two companies that meet those criteria: HCA Healthcare ( HCA 2.23%) and Vertex Pharmaceuticals ( VRTX -3.15%). Here's why their stocks could deliver better returns than ...

Precision BioSciences is a clinical-stage gene-editing company focused on the development of cell and gene therapies to treat cancer and genetic causes of disease. The company’s pipeline of ...

At Stanford, he’s trying to apply this work to detecting illness at its earliest stages, before it causes problems ... embryos to modify the gene for beta-thalassemia, a potentially deadly ...

Editas Medicine, Inc. ( NASDAQ: EDIT) Strategic Update Conference Call October 22, 2024 8:00 AM ET ...

Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) today announced that the company will present its pivotal Phase 3 data on ...

was diagnosed with Beta Thalassemia Major. He has been on monthly blood transfusions since he was six months old. Thalassemia Major is a severe, inherited blood disorder that causes low levels of ...

Not only is Casgevy designed to be a one-time functional cure for both sickle cell disease (SCD) and transfusion-dependent beta thalassemia ... the root genetic causes of APOL1-mediated kidney ...